Ionis Announces FDA Accepts New Drug Application and Grants Priority Review to Tofers for Rare, Genetic Form of ALS

SOD1-ALS is a rare genetic form of ALS that affects approximately 330 people in the US, it is progressive, leads to loss of everyday functions and is uniformly fatal If approved, tofers could be the first treatment to tackle a genetic cause of ALS 12-month data included in the application show that earlier initiation of …

Ionis Announces FDA Accepts New Drug Application and Grants Priority Review to Tofers for Rare, Genetic Form of ALS Read More »